Mixed chimeric patients, despite a limited (even
20%) engraftment, achieve a functioning graft status characterized
by normal hemoglobin level, no red blood cell transfusion requirement,
no iron increment, and a limited—not clinically relevant—
erythroid hyperplasia.31 Thus, in chimeric patients, the genetic
disease is under a substantially complete clinical control, without
achieving complete eradication of the thalassemic hemopoietic
clones
Mixed chimeric patients, despite a limited (even20%) engraftment, achieve a functioning graft status characterizedby normal hemoglobin level, no red blood cell transfusion requirement,no iron increment, and a limited—not clinically relevant—erythroid hyperplasia.31 Thus, in chimeric patients, the geneticdisease is under a substantially complete clinical control, withoutachieving complete eradication of the thalassemic hemopoieticclones
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